Advancements
Clinical Trials
Clinical trials are research studies that evaluate the safety and effectiveness of new treatments, therapies, or medical approaches for conditions like bleeding disorders. They follow a structured process with different phases, starting with small groups to assess safety and gradually involving more participants to measure effectiveness and monitor side effects. These trials are essential for advancing medical care by ensuring that new treatments are both safe and beneficial before becoming widely available. Learn more about clinical trials through the National Bleeding Disorders Foundation.
Gene Therapy
Gene therapy is an innovative approach aimed at treating or potentially curing bleeding disorders by addressing the underlying genetic causes. This therapy involves delivering a functional copy of a gene into the body to replace or repair the faulty gene responsible for a bleeding disorder. The goal is to enable the body to produce the necessary clotting factors on its own, reducing or eliminating the need for regular treatments. Learn more about gene therapy at the National Bleeding Disorders Foundation.
National Research Blueprint
The National Research Blueprint is an initiative of the National Bleeding Disorders Foundation that aims to advance the understanding, treatment, and care for those living with bleeding disorders. This comprehensive strategy focuses on identifying research priorities, promoting collaboration across medical and scientific communities, and advocating for the resources necessary to address critical gaps in knowledge and care. By driving innovation and supporting ongoing research, the Blueprint seeks to improve the lives of individuals with bleeding disorders. Learn more at the National Bleeding Disorders Foundation.